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β thalassemia

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ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)

Recruiting
  • β-thalassemia
  • β-globin restored autologous hematopoietic stem cells
  • Shenzhen, Guangdong, China
    Shenzhen University General Hospital
May 8, 2023

Thalassemia, Beta Trial in Karachi (Hydroxyurea and Thalidomide)

Completed
  • Thalassemia, Beta
  • Hydroxyurea and Thalidomide
  • Karachi, Sindh, Pakistan
    Children's Hospital Karachi
Nov 23, 2023

ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)

Recruiting
  • β-thalassemia
  • β-globin restored autologous hematopoietic stem cells
  • Shenzhen, Guangdong, China
    Shenzhen Children's Hospital
Feb 24, 2023

ß-thalassemia Trial in Shanghai (BD211)

Not yet recruiting
  • β-thalassemia
  • BD211
  • Shanghai, China
    Shanghai Ruijin Hospital
Mar 16, 2023

Beta-Thalassemia Trial (CS-101 injection)

Not yet recruiting
  • Beta-Thalassemia
  • CS-101 injection
  • (no location specified)
Sep 27, 2023

ß-thalassemia Trial (BD211)

Not yet recruiting
  • β-thalassemia
  • BD211
  • (no location specified)
Mar 15, 2023

Beta-Thalassemia Trial in Nanning (CS-101)

Recruiting
  • Beta-Thalassemia
  • CS-101
  • Nanning, China
    The First Affiliated Hospital of Guangxi Medical University
Sep 9, 2023

Pumilio1 Expression, Sickle Cell Anemia, ß-thalassemia

Not yet recruiting
  • Sickle Cell Disease, Beta Thalassemia Intermedia
  • RNA Binding Protein Pumilio1 (PUM1) Expression by reverse transcriptase quantatative PCR
  • (no location specified)
May 30, 2023

Thalassemia Major Trial (n-acetylcystine)

Not yet recruiting
  • Thalassemia Major
  • (no location specified)
Mar 9, 2023

Transfusion-dependent Beta-Thalassemia Trial in Tianjin (KL003 cell injection Drug Product)

Not yet recruiting
  • Transfusion-dependent Beta-Thalassemia
  • KL003 cell injection Drug Product
  • Tianjin, Tianjin, China
    Regenerative Medicine Center
May 8, 2023

Beta Thalassemia Major Anemia Trial (SP-420)

Not yet recruiting
  • Beta Thalassemia Major Anemia
  • (no location specified)
Jan 20, 2023

Pulmonary Functions and Physical Fitness in ß-thalassemia

Recruiting
  • β-Thalassemia
  • +2 more
  • no intervention
  • Cairo, Egypt
    Esraa Elsayed
Aug 8, 2022

The Prevelence of HBB c.93-21 G-A in ß Thalassemia Patients

Recruiting
  • Beta-Thalassemia
  • ARMS PCR
  • Assiut, Egypt
    Faculty of Medicine Assiut University
Jan 30, 2023

Thalassemia, Beta, Thalassemia Major Trial in Tianjin (VGB-Ex01)

Not yet recruiting
  • Thalassemia, Beta
  • Thalassemia Major
  • VGB-Ex01
  • Tianjin, Tianjin, China
    Regenerative Medicine Center
Sep 11, 2023

Beta-thalassemia Trial in Nanning (Luspatercept, Placebo)

Recruiting
  • Beta-thalassemia
  • Nanning, China
  • +1 more
Jan 13, 2023

Transfusion Dependent Beta-Thalassemia Trial in Nanning (GMCN-508B (LentiRed))

Recruiting
  • Transfusion Dependent Beta-Thalassemia
  • GMCN-508B (LentiRed)
  • Nanning, Guangxi, China
    The affiliated hospital of guangxi medical university
Feb 28, 2023

Luspatercept in Korean Myelodysplastic Syndrome or ß-thalassemia

Not yet recruiting
  • Myelodysplastic Syndrome
  • Beta Thalassemia
  • Seoul, Korea, Republic of
    Bristol-Myers Squibb YH
Oct 3, 2023

ß Thalassemia Major Trial in Shanghai (?-globin reactivated autologous hematopoietic stem cells)

Active, not recruiting
  • β Thalassemia Major
  • γ-globin reactivated autologous hematopoietic stem cells
  • Shanghai, Shanghai, China
    Shanghai Bioray Laboratories Inc.
Oct 9, 2022

Beta-Thalassemia Trial in China (BRL-101)

Recruiting
  • Beta-Thalassemia
  • Guangzhou, Guangdong, China
  • +3 more
Nov 7, 2022

Thalassemia Major, Transfusion-dependent Anemia Trial in Guangzhou (Luspatercept Injectable Product)

Recruiting
  • Thalassemia Major
  • Transfusion-dependent Anemia
  • Luspatercept Injectable Product
  • Guangzhou, Guangdong, China
    The second affiliated hospital of Sun Yat-sen University
Jul 15, 2022

Sickle Cell Disease, Sickle Cell Trait, Beta-Thalassemia Trial (High performance liquid chromatography, Automated sickling test,

Not yet recruiting
  • Sickle Cell Disease
  • +4 more
  • High performance liquid chromatography
  • +5 more
  • (no location specified)
Aug 17, 2022

Transfusion Dependent Beta-Thalassaemia Trial in Nanning (ET-01)

Recruiting
  • Transfusion Dependent Beta-Thalassaemia
  • ET-01
  • Nanning, Guangxi, China
    PLA 923 Hospital
Mar 2, 2023

Beta-Thalassemia, Thalassemia, Genetic Diseases, Inborn Trial in Nashville (CTX001)

Recruiting
  • Beta-Thalassemia
  • +4 more
  • CTX001
  • Nashville, Tennessee
  • +5 more
Feb 2, 2023

Beta-Thalassemia, Thalassemia, Hematologic Diseases Trial (CTX001)

Not yet recruiting
  • Beta-Thalassemia
  • +6 more
  • CTX001
  • (no location specified)
Jul 26, 2022

The Prevelence of IVS 1-6 [HBB:c.92 +6 T-C] Gene Mutation in

Not yet recruiting
  • Beta-Thalassemia
  • ARMS
  • (no location specified)
May 10, 2022